LONG-TERM EFFICACY AND SAFETY OF THE ORAL PYRUVATE KINASE ACTIVATOR MITAPIVAT IN ADULTS WITH NON–TRANSFUSION-DEPENDENT ALPHA- OR BETA-THALASSEMIA.

KH Kuo, DM Layton, A Lal, H Al-Samkari, J Bhatia, PA Kosinski, B Tong, M Lynch, K Uhlig, EP Vichinsky. LONG-TERM EFFICACY AND SAFETY OF THE ORAL PYRUVATE KINASE ACTIVATOR MITAPIVAT IN ADULTS WITH NON–TRANSFUSION-DEPENDENT ALPHA- OR BETA-THALASSEMIA. Hematology Transfusion and Cell Therapy. 2022 Oct 1; 44:s11-s12.

2022
https://researcherprofiles.org/profile/425025953

KH Kuo, DM Layton, A Lal, H Al-Samkari, J Bhatia, PA Kosinski, B Tong, M Lynch, K Uhlig, EP Vichinsky